MEDIA

Mila's Miracle Foundation has gained national and international press attention as we have worked tirelessly on paths to a cure for devastating neurological conditions like Batten.

Click the icons below to view recent media coverage on Mila’s Miracle Foundation.

MEDIA ARCHIVES

• The New England Journal of Medicine, "Patient-Customized Oligonucleotide Therapy for a Rare Genetic Disease"

• The New England Journal of Medicine, "Drug Regulation in the Era of Individualized Therapies"

• Science Magazine, "Drug tailored to one girl with brain disease paves way for similar customized treatments"

• The New York Times, "Scientists Designed a Drug for Just One Patient. Her Name Is Mila."

• MIT Technology Review, "This girl’s dramatic story shows hyper-personalized medicine is possible—and costly"

• STAT, "After a bespoke therapy rescues a young girl, the FDA considers advance of individualized treatments"

• MedPage Today, "Mila's N-of-1 Trial Detailed in NEJM"

• 90.9 WBUR Boston, "A Drug Was Made For Just One Child, Raising Hopes About Future Of Tailored Medicine"

• Batten Disease News, "Customized Oligonucleotides Treat Seizures in Child with CLN7 Disease in Record Time"

• Eureka, "Medicine for Mila: How physicians and scientists teamed up for one little girl born with a deadly form of Batten disease"

• Fox News, "Girl facing fatal brain disease gets tailor-made drug"

• Advisory Board, "Meet 'Milasen': The first-ever drug designed for just one patient"

• BBC News, "Batten disease girl given custom-made drug"

• Daily Mail, "'She's still herself': Girl, 8, left blind and mute by an incurable rare brain disease is the first patient to get a drug tailor-made - and named - for her in historic step for personal medicine"

• Süddeutsche Zeitung, "Ein Medikament nur für Mila"

• de Volkskrant, "Amerikaanse artsen maken genetisch medicijn voor één meisje"

• Le Monde, "Un traitement ultra-personnalisé pour une fillette souffrant d’une maladie génétique rare"

• la Repubblica, "Per la prima volta messo a punto farmaco per un singolo paziente"

• Corriere Della Sera, "Farmaco creato per una sola paziente Mila, 8 anni, ha la malattia di Batten"

• FanPage.it, "Creato farmaco rivoluzionario per trattare un singolo paziente con una rarissima malattia genetica"

• Quotidiano.net, "Creato farmaco per una sola paziente: cura per una bimba con la malattia di Batten"

• L’HuffPost, "Scienziati creano un farmaco per una sola paziente: Mila, 8 anni, ha una sindrome rarissima"

• Open, "Nuovo farmaco sperimentato su Mila, la bimba affetta dal morbo di Batten. Ma attenzione a non dare false speranze"

• Il Post, "Il primo farmaco creato per un solo paziente"

• Nurse Times, "Boston, creato un farmaco personalizzato per curare la piccola Mila"

• Il Tempo, "Scienziati Usa creano il primo farmaco per una sola persona al mondo"

• Sputnik Italia, "USA, equipe di scienziati brevetta cura per una sola paziente"

• El País Espana, "Creado por primera vez un fármaco para un único paciente: una niña con una enfermedad letal"

• ABC España, "Milasen: el primer fármaco ‘personalizado’ que salva a la niña con una enfermedad cerebral mortal"

• 20 Minutos, "Crean un fármaco para un único paciente: una niña con una enfermedad mortal"

• Televisió de Catalunya 324, "Creen un fàrmac per a un sol pacient: una nena amb una malaltia mortal"

• Athens Voice, "Εξατομικευμένο φάρμακο για μία και μόνο ασθενή, δίνει ελπίδα σε πολλούς"

• Nooz, "Ανοίγει ο δρόμος της εξατομικευμένης ιατρικής- Το παράδειγμα "Μίλα"

• Parallaxi Mag, "Επιστήμονες δημιούργησαν νέο φάρμακο σώζοντας ένα κοριτσάκι με θανατηφόρα νόσο"

• JutarnjiLife, "DOKTORI OSMISLILI NOVI LIJEK SAMO ZA NJU Priča o teško oboljeloj Mili Makovec: 'Pomislili smo da joj možemo pomoći i napravili smo lijek Milasen...'"

• WuXi PharmaTech, "这些只能治疗一名患者的疗法，或将带来个体化医疗的新时代"

• Caixin, " 解药｜世界首例个人定制药物是如何问世的"

• ScienceNet.cn, "定制药物治疗脑病见成效"

• HeHo Health, "[全球第一] 讓9歲的女孩有活下去的權力 科學家量身打造新藥「個性化治療」揭開里程碑"

• India Times, " सिर्फ एक मरीज के इस्तेमाल के लिए बनाई गई खास दवा"

• The Alayaran, "US doctors customise drug to treat girl with rare genetic disease"

• Gulf News, "A drug invented for just one patient"

• Live Science, "Girl Diagnosed with Fatal Brain Disease Gets a Tailor-Made Drug within a Year"

• Pink Sheet, "One Patient, Many Questions: Milasen ‘N of 1’ Trial Provides Early Template For Individualized Genomic Medicine"

• EurekAlert!, "New customized drug treatment bypasses a single child's unique mutation within a year of diagnosis"

• CTV News, "Eight-year-old girl gets personalized drug for rare disease after parents raise millions"

• Science Codex, "New customized drug treatment bypasses a single child's unique mutation within a year of diagnosis"

• Health Gazette, "Scientists designed a drug for just one patient. Her name is Mila."

• Clinical OMICs, "BCH N of 1 Trial Yields Approved Therapy for Single Rare Disease Patient"

• Guru Online News, "Unique drug for a girl with deadly brain disease"

• Nature Medicine, "Antisense therapies pose a regulatory conundrum"

• MedPage Today, "Desperate Families Pursue 'N-of-1' Trials for Ultra-Rare Diseases"

• Boston Children’s Hospital Trust, Spirit of Giving, The Dare Issue, "In Rare Form"

• NeurologyToday, "An Antisense Oligonucleotide Therapy Looks Promising for a Rare Form of Batten Disease"

• Left Hand Valley Courier, "Mila’s Miracle featured at CU’s GoldLab Symposium"

• Chemical & Engineering News, "Have antisense oligonucleotides hit their stride?"

• BioQuick News, "Patient-Customized Anti-Sense Therapy Possibly Successful for Young Girl with MFSD8/CLN7 Batten Disease, an Ultra-Rare and Generally Fatal Genetic Disease"

• Fox 5 DC, "New customized drug is giving young girl suffering from rare brain disease new hope for cure"

• The Boston Globe, "Saving Mila: How a tailor-made therapy, developed in a flash, may have halted a young girl’s rare disease"

• STAT, "Saving Mila: How a tailor-made therapy, developed in a flash, may have halted a young girl’s rare disease"

• Science Magazine, “A tailormade drug developed in record time may save girl from fatal brain disease”

• Daily Mail, “World first as experimental drug appears to REVERSE symptoms in girl, 7, with incurable disease that causes paralysis, blindness, dementia and early death”

• MIT Technology Review, “Gene treatment made for a single child cuts a hyper-personal path for precision medicine”

• Inquisitr, “Record Drug Development May Save Girl From Fatal Brain Disease”

• Patient Worthy, "A Girl From Colorado is Receiving An Experimental Treatment for Her Batten Disease"

• Left Hand Valley Courier, "Mila starts leading-edge treatment"

• Times-Call, "Boulder County girl undergoing experimental treatment for Batten disease"

• Boulder Patch, "Batten Disease: Gene Therapy Offers Hope for Boulder Girl"

• Boulder Lifestyle, "Finding a Miracle"

• Forbes, "Rapper B.o.B Just Started A GoFundMe To Prove The Earth Is Flat"

• Times-Call, "Boulder County family down to wire in fight against rare disease"

• Buzz.ie, "Family must raise $1M to save their 6-year-old daughter's life"

• Fox 31, "Boulder family races to raise $1 million for clinical trial for daughter’s deadly disease"

• New York Post, "Family races to save 6-year-old with fatal genetic disease"

• Fox 31, "Family racing to raise funds for daughter facing incurable genetic disease"

• Today Show, "Parents of little girl with rare, deadly disease race time to save her"

• Climbing, "Mila Makovec: A Little Climber in Need of Our Help"

• Times-Call, "Boulder County family is funding race against deadly Batten disease"

• Fox 31, "Governor’s wife joins fight to help family raise $4 million for clinical trial"

• Fox 31, "Teachers school each other to help families’ wishes come true"

• Fox 31, "Charity steps up to help family raise $4 million to find cure for daughter’s deadly disease"

• Daily Mail, "Tragedy of Girl, 6, Who Suffers from Rare Disease that Will Rob Her of Speech, Mobility and Eyesight — and Could Kill Her Before She's a Teen"

• The Denver Post, "Family’s struggle with Batten disease mirrors the journey of others fighting rare diseases"

• Fox 31, "Family trying to raise millions to fight daughter’s rare, deadly disease"

• Daily Camera Longmont News, "Boulder County family desperate to raise money to combat rare Batten disease"

• Daily Camera, "Photos: Boulder County Girl Diagnosed with Batten Disease"

• ABC Denver 7, "Longmont girl battles rare disease with no cure in sight"

For media inquiries, contact Julia Vitarello.